Filtros de búsqueda

Lista de obras de

A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells

scientific article published on 06 August 2018

Allogeneic stem cell transplantation in adolescents and young adults with primary immunodeficiencies

artículo científico publicado en 2017

Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells

article

Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells

artículo científico publicado en 2019

Gene correction for SCID-X1 in long-term hematopoietic stem cells

article

Genome editing of donor-derived T-cells to generate allogenic chimeric antigen receptor-modified T cells: Optimizing αβ T cell-depleted haploidentical hematopoietic stem cell transplantation

scientific article published on 02 April 2020

Highly Efficient and Marker-free Genome Editing of Human Pluripotent Stem Cells by CRISPR-Cas9 RNP and AAV6 Donor-Mediated Homologous Recombination

artículo científico publicado en 2019

IPEX due to an exon 7 skipping FOXP3 mutation with autoimmune diabetes mellitus cured by selective TReg cell engraftment

artículo científico publicado en 2018

MRD response in a refractory paediatric T-ALL patient through anti-programmed cell death 1 (PD-1) Ab treatment associated with induction of fatal GvHD.

artículo científico publicado en 2017

Maturation of Platelet Function During Murine Fetal Development In Vivo.

artículo científico publicado en 2017

Metabolic engineering generates a transgene-free safety switch for cell therapy

scientific article published on 13 July 2020

Organic nitrates differentially modulate circulating endothelial progenitor cells and endothelial function in patients with symptomatic coronary artery disease

artículo científico publicado en 2011

Reduced toxicity, myeloablative HLA-haploidentical hematopoietic stem cell transplantation with post-transplantation cyclophosphamide for sickle cell disease

artículo científico publicado en 2017

T-cell replete haploidentical bone marrow transplantation and post-transplant cyclophosphamide for patients with inborn errors

artículo científico publicado en 2019

Tuning the Antigen Density Requirement for CAR T Cell Activity

artículo científico publicado en 2020