Lista de obras -

A DL-4- and TNFα-based culture system to generate high numbers of nonmodified or genetically modified immunotherapeutic human T-lymphoid progenitors

artículo científico publicado en 2021

A Nontoxic Transduction Enhancer Enables Highly Efficient Lentiviral Transduction of Primary Murine T Cells and Hematopoietic Stem Cells

artículo científico publicado en 2018

A combination of cyclophosphamide and interleukin-2 allows CD4+ T cells converted to Tregs to control scurfy syndrome

artículo científico publicado en 2021

A gain-of-function RAC2 mutation is associated with bone-marrow hypoplasia and an autosomal dominant form of severe combined immunodeficiency

artículo científico publicado en 2020

AK2 deficiency compromises the mitochondrial energy metabolism required for differentiation of human neutrophil and lymphoid lineages

artículo científico publicado en 2015

An in vivo genetic reversion highlights the crucial role of Myb-Like, SWIRM, and MPN domains 1 (MYSM1) in human hematopoiesis and lymphocyte differentiation

artículo científico publicado en 2015

Baboon envelope LVs efficiently transduced human adult, fetal, and progenitor T cells and corrected SCID-X1 T-cell deficiency

artículo científico publicado en 2019

Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID

scientific article published on 13 September 2019

Competition within the early B-cell compartment conditions B-cell reconstitution after hematopoietic stem cell transplantation in nonirradiated recipients

article

Concurrent engagement of CD40 and the antigen receptor protects naive and memory human B cells from APO-1/Fas-mediated apoptosis

artículo científico publicado en 1996

Correction of murine Rag1 deficiency by self-inactivating lentiviral vector-mediated gene transfer.

artículo científico publicado en 2011

Disruption of the lineage restriction of TCR beta gene rearrangements.

artículo científico publicado en 2002

Fas-dependent and Fas-independent mechanisms for selection of the mature human B cell repertoire.

artículo científico publicado en 1997

Gene Therapy with Hematopoietic Stem Cells: The Diseased Bone Marrow's Point of View.

artículo científico publicado en 2016

Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency

artículo científico publicado en 2017

Gene-corrected human Munc13-4-deficient CD8+ T cells can efficiently restrict EBV-driven lymphoproliferation in immunodeficient mice.

artículo científico publicado en 2016

Hematopoietic Stem Cell Transplant for the Treatment of X-MAID

artículo científico publicado en 2019

Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome

artículo científico publicado en 2022

Medical perspectives of adults and embryonic stem cells

scientific article published on 01 October 2002

NHP2 deficiency impairs rRNA biogenesis and causes pulmonary fibrosis and Høyeraal-Hreidarsson syndrome

scientific article published on 27 January 2020

Occurrence of myelodysplastic syndrome in 2 patients with reticular dysgenesis