Lista de obras - Salima Hacein-Bey-Abina - Dominio Público Uruguay

20 years of gene therapy for SCID.

artículo científico publicado en 2010

A method to sequence and quantify DNA integration for monitoring outcome in gene therapy ⬇️

artículo científico publicado en 2011

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

artículo científico publicado en 2014

A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells

artículo científico publicado en 2010

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

artículo científico publicado en 2003

Advances in adoptive immunotherapy to accelerate T-cellular immune reconstitution after HLA-incompatible hematopoietic stem cell transplantation

artículo científico publicado en 2010

Clonal evidence for the transduction of CD34+ cells with lymphomyeloid differentiation potential and self-renewal capacity in the SCID-X1 gene therapy trial

artículo científico publicado en 2004

Cytokines and culture medium have a major impact on human in vitro T-cell differentiation

artículo científico publicado en 2011

DNA bar coding and pyrosequencing to analyze adverse events in therapeutic gene transfer

artículo científico publicado en 2008

Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial

artículo científico publicado en 2010

Efficacy of gene therapy for X-linked severe combined immunodeficiency

artículo científico publicado en 2010

Failure of SCID-X1 gene therapy in older patients

artículo científico publicado en 2005

Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1.

artículo científico publicado en 2015

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

artículo científico publicado en 2016

Gene Therapy in a Patient with Sickle Cell Disease

artículo científico publicado en 2017

Gene therapy for immunodeficiency diseases

artículo científico publicado en 2004

Gene therapy for inherited immunodeficiency

artículo científico publicado en 2014

Gene therapy for primary adaptive immune deficiencies

artículo científico publicado en 2011

Gene therapy for primary immunodeficiencies

artículo científico publicado en 2010

Gene therapy for primary immunodeficiencies.

artículo científico publicado en 2015

Gene therapy for primary immunodeficiencies: Part 1.

artículo científico

Gene therapy for severe combined immunodeficiency

artículo científico publicado en 2005

Gene therapy of X-linked severe combined immunodeficiency

artículo científico publicado en 2002

Gene therapy of metabolic diseases

artículo científico publicado en 2006

Gene therapy of primary T cell immunodeficiencies

artículo científico

Gene therapy: X-SCID transgene leukaemogenicity

artículo científico publicado en 2006

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

artículo científico publicado en 2009

INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes

artículo científico publicado en 2016

Immune reconstitution after haematopoietic stem cell transplantation: obstacles and anticipated progress

artículo científico publicado en 2009

Improving immune reconstitution while preventing graft-versus-host disease in allogeneic stem cell transplantation

artículo científico publicado en 2002

Insertion sites in engrafted cells cluster within a limited repertoire of genomic areas after gammaretroviral vector gene therapy

artículo científico publicado en 2011

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

artículo científico publicado en 2008

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

artículo científico publicado en 2011

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

artículo científico publicado en 2003

Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy

artículo científico publicado en 2012

Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency

artículo científico publicado en 2009

Loss of p19Arf in a Rag1(-/-) B-cell precursor population initiates acute B-lymphoblastic leukemia

artículo científico publicado en 2011

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome

artículo científico publicado en 2015

Real-time definition of non-randomness in the distribution of genomic events

artículo científico publicado en 2007

Restoration of human B-cell differentiation into NOD-SCID mice engrafted with gene-corrected CD34+ cells isolated from Artemis or RAG1-deficient patients

artículo científico publicado en 2007

Severe combined immunodeficiency. A model disease for molecular immunology and therapy

artículo científico publicado en 2005

Site- and allele-specific polycomb dysregulation in T-cell leukaemia

artículo científico publicado en 2015

Specific T cells for the treatment of cytomegalovirus and/or adenovirus in the context of hematopoietic stem cell transplantation

artículo científico publicado en 2016

Stem cell self-renewal: lessons from bone marrow, gut and iPS toward clinical applications

artículo científico publicado en 2011

Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID).

artículo científico publicado en 2012

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

artículo científico publicado en 2002

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

artículo científico publicado en 2010

Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia

artículo científico publicado en 2005

Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy

artículo científico publicado en 2007

Lista de obras de Salima Hacein-Bey-Abina

20 years of gene therapy for SCID.

A method to sequence and quantify DNA integration for monitoring outcome in gene therapy ⬇️

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

Advances in adoptive immunotherapy to accelerate T-cellular immune reconstitution after HLA-incompatible hematopoietic stem cell transplantation

Clonal evidence for the transduction of CD34+ cells with lymphomyeloid differentiation potential and self-renewal capacity in the SCID-X1 gene therapy trial

Cytokines and culture medium have a major impact on human in vitro T-cell differentiation

DNA bar coding and pyrosequencing to analyze adverse events in therapeutic gene transfer

Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial

Efficacy of gene therapy for X-linked severe combined immunodeficiency

Failure of SCID-X1 gene therapy in older patients

Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1.

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

Gene Therapy in a Patient with Sickle Cell Disease

Gene therapy for immunodeficiency diseases

Gene therapy for inherited immunodeficiency

Gene therapy for primary adaptive immune deficiencies

Gene therapy for primary immunodeficiencies

Gene therapy for primary immunodeficiencies.

Gene therapy for primary immunodeficiencies: Part 1.

Gene therapy for severe combined immunodeficiency

Gene therapy of X-linked severe combined immunodeficiency

Gene therapy of metabolic diseases

Gene therapy of primary T cell immunodeficiencies

Gene therapy: X-SCID transgene leukaemogenicity

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes

Immune reconstitution after haematopoietic stem cell transplantation: obstacles and anticipated progress

Improving immune reconstitution while preventing graft-versus-host disease in allogeneic stem cell transplantation

Insertion sites in engrafted cells cluster within a limited repertoire of genomic areas after gammaretroviral vector gene therapy

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy

Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency

Loss of p19Arf in a Rag1(-/-) B-cell precursor population initiates acute B-lymphoblastic leukemia

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome

Real-time definition of non-randomness in the distribution of genomic events

Restoration of human B-cell differentiation into NOD-SCID mice engrafted with gene-corrected CD34+ cells isolated from Artemis or RAG1-deficient patients

Severe combined immunodeficiency. A model disease for molecular immunology and therapy

Site- and allele-specific polycomb dysregulation in T-cell leukaemia

Specific T cells for the treatment of cytomegalovirus and/or adenovirus in the context of hematopoietic stem cell transplantation

Stem cell self-renewal: lessons from bone marrow, gut and iPS toward clinical applications

Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID).

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia

Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy